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How an Ohio Kids' Hospital Quietly Became Ground Zero for Gene Therapy

HOW AN OHIO KIDS' HOSPITAL QUIETLY BECAME GROUND ZERO FOR GENE THERAPY

If a once-modest regional hospital and its new biotech allies have their way, the capital of Ohio could one day rival America's other...

 
 
 
15 For '19: Key Clinical Data to Watch For Next Year

15 FOR '19: KEY CLINICAL DATA TO WATCH FOR NEXT YEAR

On Monday, Xconomy began our annual look ahead at clinical trials that could define biotech and have profound healthcare effects in...

 
 
 
Spinraza Inventors Take Home $3M Breakthrough Prize in Life Sciences

SPINRAZA INVENTORS TAKE HOME $3M BREAKTHROUGH PRIZE IN LIFE SCIENCES

The inventor and developer of a drug, nusinersen , are among the winners of the Breakthrough Prize in Life Sciences. Adrian Krainer...

 
 
 
Bio Roundup: Nobel Prizes, Duchenne Steps, Guardant's IPO & More

BIO ROUNDUP: NOBEL PRIZES, DUCHENNE STEPS, GUARDANT'S IPO & MORE

Cancer immunotherapy is all the rage these days. The idea of harnessing the immune system to treat cancer has sparked billions of dollars...

Bio Roundup: Big Approvals, ICER Influence, Drug-Price Pushback & More

BIO ROUNDUP: BIG APPROVALS, ICER INFLUENCE, DRUG-PRICE PUSHBACK & MORE

We'll start the roundup this week with two drug approvals that came late last Friday. Both were landmarks for the companies receiving...

 
 
 
 
 
 
 
 
 
 
 
 
 
 
 
 
 
 

BIOGEN SETS $750,000 INITIAL PRICE FOR FIRST-EVER SPINAL ATROPHY DRUG

Patients with spinal muscular atrophy got some good news last week when the FDA approved nusinersen , making it the first marketed...

FDA Approves Nusinersen Drug To Treat Spinal Muscular Atrophy

FDA APPROVES NUSINERSEN DRUG TO TREAT SPINAL MUSCULAR ATROPHY

The United States Food and Drug Administration has recently approved Nusinersen drug to treat Spinal Muscular Atrophy.