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Decision on spinal muscular atrophy treatment Spinraza deferred

DECISION ON SPINAL MUSCULAR ATROPHY TREATMENT SPINRAZA DEFERRED

Pharmac subcommittee says it wants more evidence before it commits to a $1 million treatment for spinal muscular atrophy.

15 For '19: Key Clinical Data to Watch For Next Year

15 FOR '19: KEY CLINICAL DATA TO WATCH FOR NEXT YEAR

On Monday, Xconomy began our annual look ahead at clinical trials that could define biotech and have profound healthcare effects in...

 
 
 
Bio Roundup: Alzheimer's Puzzle, ESMO Assessed, Drug Prices & More

BIO ROUNDUP: ALZHEIMER'S PUZZLE, ESMO ASSESSED, DRUG PRICES & MORE

In the biotech investment and research communities this week, much of the attention was turned to Europe. Munich, Germany, hosted the...

 
 
 
Parents urge officials to approve drugs to treat the condition crippling their five-year-old son 

PARENTS URGE OFFICIALS TO APPROVE DRUGS TO TREAT THE CONDITION CRIPPLING THEIR FIVE-YEAR-OLD SON 

EXCLUSIVE: Finley Newell, from Haddenham in Buckinghamshire, has spinal muscular atrophy which could be treated with the drug Spinraza...

Bio Roundup: Prices on TV, Novartis Hearts Radio, Warp Drive's End

BIO ROUNDUP: PRICES ON TV, NOVARTIS HEARTS RADIO, WARP DRIVE'S END

Two new battlegrounds emerged this week in the nation's ongoing drug pricing debate. The first involved television: The federal government...

 
 
 
Spinraza Inventors Take Home $3M Breakthrough Prize in Life Sciences

SPINRAZA INVENTORS TAKE HOME $3M BREAKTHROUGH PRIZE IN LIFE SCIENCES

The inventor and developer of a drug, nusinersen , are among the winners of the Breakthrough Prize in Life Sciences. Adrian Krainer...

Bio Roundup: Big Approvals, ICER Influence, Drug-Price Pushback & More

BIO ROUNDUP: BIG APPROVALS, ICER INFLUENCE, DRUG-PRICE PUSHBACK & MORE

We'll start the roundup this week with two drug approvals that came late last Friday. Both were landmarks for the companies receiving...

 
 
 

WITH TECH FROM SPINRAZA'S MAKER, FRENCH STARTUP DYNACURE GETS $55M TO TACKLE NEUROMUSCULAR DISEASE

Drug discovery powerhouse Ionis gave Biogen one of its biggest wins in recent times with the delivery of Spinraza, the spinal muscular...

 
 
 
 
 
 
New Gene Therapy Medication can Treat Muscle Disease in Children

NEW GENE THERAPY MEDICATION CAN TREAT MUSCLE DISEASE IN CHILDREN

Spinraza, a new advanced gene therapy medication can be used to treat severe form of neuromuscular disease like spinal muscular atrophy...

 
 
 
Biogen boosts its outlook after a blockbuster quarter

BIOGEN BOOSTS ITS OUTLOOK AFTER A BLOCKBUSTER QUARTER

REUTERS/Brian Snyder - Biogen Inc's second-quarter profit smashed estimates on Tuesday, boosted by strong sales of its spinal muscular...