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FDA gives thumbs down to Sarepta's next Duchenne's muscular dystrophy drug

FDA GIVES THUMBS DOWN TO SAREPTA'S NEXT DUCHENNE'S MUSCULAR DYSTROPHY DRUG

The decision stood in contrast with the agency's highly controversial approval of Sarepta's previous DMD drug, Exondys 51. The company's...

When Size Matters: Using SMRT Sequencing to Help Patients With Repeat Expansion Disorders 

WHEN SIZE MATTERS: USING SMRT SEQUENCING TO HELP PATIENTS WITH REPEAT EXPANSION DISORDERS 

Patients with myotonic dystrophy type 1 want to know their size - the size of the expansion of repeats of the unstable CTG sequences...

 
 
 
Analysts grill Novartis execs amid gene therapy data manipulation scandal

ANALYSTS GRILL NOVARTIS EXECS AMID GENE THERAPY DATA MANIPULATION SCANDAL

Novartis CEO Vas Narasimhan said the data manipulation issue was confined to a disused potency assay for use in mice and predated the...

 
 
 
 
 
 
Bio Roundup: Michael Becker, Suzanne Eaton, Gene Therapy Moves & More

BIO ROUNDUP: MICHAEL BECKER, SUZANNE EATON, GENE THERAPY MOVES & MORE

The life science and healthcare worlds are vast. We often talk about impact in terms of millions of patients and billions of dollars....

PFIZER'S DMD GENE THERAPY SAFETY DATA HAND ADVANTAGE TO SAREPTA

An early clinical update on Pfizer's Duchenne muscular dystrophy gene therapy has raised safety concerns. One of the first six people...

 
 
 
I Didn't Know How Much I Needed This Video of Tom Holland Cuddling With Rescue Puppies

I DIDN'T KNOW HOW MUCH I NEEDED THIS VIDEO OF TOM HOLLAND CUDDLING WITH RESCUE PUPPIES

Tom Holland is undoubtedly adorable on his own , but put some puppies in those muscular arms of his , and goodness gracious, it's simply...

Teen Mom's Mackenzie McKee Fires Back at Body-Shamer After Showing Off Her Killer Figure

TEEN MOM'S MACKENZIE MCKEE FIRES BACK AT BODY-SHAMER AFTER SHOWING OFF HER KILLER FIGURE

Bye, troll! Teen Mom star Mackenzie McKee shut down a body-shamer who commented on her muscular physique. The reality starlet is feeling...

 
 
 
Bio Roundup: Opioids in Court, IPO Parade, Brain Cancer Bet & More

BIO ROUNDUP: OPIOIDS IN COURT, IPO PARADE, BRAIN CANCER BET & MORE

Pharmaceutical companies that make or market opioids have found themselves in legal hot water, and much of the heat is coming from...

People using Tinder and other dating apps are 'more likely to use steroids'

PEOPLE USING TINDER AND OTHER DATING APPS ARE 'MORE LIKELY TO USE STEROIDS'

Scientists at Harvard University said pressure is growing on people to look like celebrities. Pictured, Love Island contestant Anton...

 
 
 

AVEXIS RECEIVES FDA APPROVAL FOR ZOLGENSMA, FIRST AND ONLY GENE THERAPY FOR PEDIATRIC PATIENTS WITH SPINAL MUSCULAR ATROPHY

Posted on: 25 May 2019, AveXis, a Novartis company, today announced the US Food and Drug Administration has approved Zolgensma® for...

 
 
 

SOLID TANKS AS SAFETY SCARE AGAIN ROCKS DMD GENE THERAPY

A safety scare has rocked Solid Biosciences' drive to get its Duchenne muscular dystrophy gene therapy program back on track. The first...